In the context of EJP RD’s ERN Workshops, a face-to-face workshop entitled “Epidermolysis bullosa: from genes to translation into therapies” is being organized by Prof. [...]
As part of the training activities proposed by the EJP RD, a 2h30 training course titled “The Statistical Evaluation of Surrogate Endpoints in Clinical Trials” [...]
Through the last decade access to modern healthcare has improved significantly. The lack of scientific knowledge about rare diseases (RDs) often results in a delay [...]
IRDiRC, a global collaborative initiative with the vision to enable all people living with a rare disease to receive an accurate diagnosis, care, and available [...]
