EMA Webinar on Rare World Diseases Day

EMA RD Day webinar

Orphan Medicines Development – ask the European regulator

Thursday, 29 February 2024 Virtual meeting via WebEx / EMA, Amsterdam

The EMA’s Orphan Medicines Office is hosting an interactive webinar on Rare Disease Day on 29 February 2024, to answer questions that developers of products for rare diseases or researchers in this field might have on orphan designations and rare disease development. The webinar will feature:

  • short presentations on the background of orphan designation and the benefits it has brought to patients;
  • a live question-and-answer session enabling participants to ask their questions on orphan medicines development to a panel of regulatory experts.

More info: Orphan medicines development – ask the European regulator | European Medicines Agency (europa.eu)

View this webinar

Webinar summary

WebinarEMA Webinar on Rare World Diseases Day
DateFebruary 29th, 2024
Time16:00 – 17:25 hr
SpeakersKristina Larsson (Head of Orphan Medicines Office (EMA) )
Virginie Hivert (EURORDIS)
Melanie Carr (Head of Stakeholders and Communication (EMA))
Hélène Le Borgne ( EC, Directorate General for Research and Innovation)
Theodor Framke ( EMA, clinical trial methodology )
Violeta Stoyanova-Beninska (MEB, COMP Chair )
Iordanis Gravanis (EMA, scientific advice and protocol assistance )
Maria Mavris (EMA, patient engagement )
Maribel Rico-Salas (EMA, academia liaison )
WebsiteVisit webinar website
RegistrationRegistration is closed