Is transthyretin amyloid cardiomyopathy heading towards losing its rare disease classification?

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TitleIs transthyretin amyloid cardiomyopathy heading towards losing its rare disease classification?
Date2025-01-01
Issue nameExpert review of cardiovascular therapy
Issue numberv23.1-2:1-4
DOI10.1080/14779072.2025.2463333
PubMed39928028
AuthorsAchten A, Muller SA, Zwetsloot PP, Michels M, van der Meer P, Nienhuis HLA, van der Meer MG, van Empel VPM, Oerlemans MIFJ & Knackstedt C
KeywordsATTR, amyloid, amyloidosis, cardiomyopathy, genetic
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