#Research

EMA Webinar on Rare World Diseases Day

This webinar took place on February 29th, 2024
EMA RD Day webinar

Orphan Medicines Development – ask the European regulator

Thursday, 29 February 2024 Virtual meeting via WebEx / EMA, Amsterdam

The EMA’s Orphan Medicines Office is hosting an interactive webinar on Rare Disease Day on 29 February 2024, to answer questions that developers of products for rare diseases or researchers in this field might have on orphan designations and rare disease development. The webinar will feature:

short presentations on the background of orphan designation and the benefits it has brought to patients; a live question-and-answer session enabling participants to ask their questions on orphan medicines development to a panel of regulatory [...]

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MOOC 2: Diagnosing Rare Diseases: From The Clinic To Research And Back

Posted on
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We are thrilled to announce a new session of the online course “diagnosing rare diseases: from the clinic to research and back”, which will be offered for free !

Participants will learn about diagnostic research progress, types of genetic tests for rare diseases, and the impact of having or lacking a diagnosis on patients’ lives over 5 weeks. They will also explore rare genetic disease issues and conduct an internet-based investigation on diagnostic research topics. The weekly content is 3 hours, and learners will receive cutting-edge insights.

Expert mentors will be readily available on the platform to address any questions [...]

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